Gene therapy

Here’s the best, most inspiring and coolest science we encountered this year

From new uses for weight-loss drugs to the first CRISPR gene editing therapy, these were some of the most impactful health stories of the year

Most people with sickle cell disease who received a new gene editing treatment saw their pain resolve for at least one year, but longer follow up is needed

A newly approved CRISPR therapy could transform the treatment of sickle cell disease and beta-thalassemia—but the technology is expensive

A new book argues that genomics is overshadowing environmental and social solutions to better health for all

The treatment will be reviewed by an outside panel this week

The gene therapy could save kids with severe combined immune deficiency

Gene-editing technique to treat lung cancer is due to be tested in people in August

Economists, investors and medical insurers can’t figure out how to pay for cutting-edge drugs

Progressive supranuclear palsy has become a test bed for therapies aimed at the tau protein thought to be behind many devastating neurodegenerative disorders

Scientists use a process developed by bacteria to manipulate RNA  

A technique to stop children from inheriting mitochondrial diseases has the potential to backfire